Breakthrough Business Models: Drug Development for Rare and Neglected Diseases and Individualized Therapies: Workshop Summary
Resource Shelf (Free subscription) | 11/21/2009
From the Web Site: Orphanet is a database of information on rare diseases and orphan drugs for all publics. Its aim is to contribute to the improvement of the diagnosis, care and treatment of patients with rare diseases. Orphanet includes a Professional Encyclopaedia, which is expert-authored and peer-reviewed, a Patient Encyclopaedia and a Directory of expert [...]
PR News Wire (Free subscription) | 11/19/2009
MUNSTER, Germany, November 19 /PRNewswire/ -- MONITORING FORCE GmbH announced that they have filed on November 16th, 2009 Flibanserin in the indication treatment-relevant levodopa-induced dyskinesia in Parkinson's disease for orphan drug status designation with the European Medicines Agency (EMEA). Levodopa-induced dyskinesia is a complication of the mainstay treatment in advanced Parkinson's and a...
Red Orbit (Free subscription) | 11/19/2009
MUNSTER, Germany, November 19 /PRNewswire/ -- MONITORING FORCE GmbH announced that they have filed on November 16th, 2009 Flibanserin in the indication treatment-relevant levodopa-induced dyskinesia in Parkinson's disease for orphan drug status designation with the European Medicines Agency (EMEA).
Startup Professionals Musings (Free subscription) | 11/18/2009
In addition to the “green” sector, which I outlined a few weeks ago , I see biotech as one of the places where startups can always go for real opportunities. Recession-proof products with innovation continue to come from the biotechnology industry. Plus, it was one of the top three categories attracting VC money in the most recent quarter of 2009 . In its most general sense, biotech is...
Medical News Today (Free subscription) | 11/16/2009
Apogenix GmbH, a biopharmaceutical company developing novel drugs for malignant and inflammatory diseases, announced that the European Medicines Agency adopted a positive opinion on orphan medicinal product designation for the company's lead candidate APG101 for the treatment of Glioblastoma multifome (GBM), and that it has already been granted orphan drug status in the US by the US Food and Drug Administration...
New York Times (Free subscription) | 11/14/2009
Vials of five different Genzyme drugs for rare diseases may be contaminated with tiny particles of steel, rubber or fiber that could potentially harm patients, the Food and Drug Administration warned Friday.
Medical News Today (Free subscription) | 11/11/2009
Ikano Therapeutics, Inc. (ITI) announced that it has received Orphan Drug designation for midazolam in the acute treatment of certain forms of epileptic seizure known as cluster seizures or alternatively, as acute repetitive seizures. ITI has a nasally administered form of midazolam called ITI-111 in late stage clinical development that is aimed at the treatment of these specific seizure types in an...
Music Maza (Free subscription) | 11/11/2009
After the release of Paa, merchandise connected to the film's young protagonist Auro played by the Big B, is being planned. For the first time his younger fans will have Big B merchandise including dolls to play with. The producers, AB Corp Ltd, have planned an 'Auro' blitzkrieg to connect the character with children across the world. While a series of Auro merchandise are planned post the film's...
ABC News (Free subscription) | 11/09/2009
Orphan drug treatment used only on mice to get hearing before FDA.
Contract Pharma Breaking News (Free subscription) | 11/09/2009
Enzon Pharmaceuticals (Booth 611) will sell its specialty pharmaceutical business, including its CMO operations, to the sigma-tau Group for $300 million plus an additional amount of up to $27 million based on success milestones. Enzon will also receive royalties of 5 to 10% on incremental net sales above a 2009 baseline amount from Enzon’s four marketed specialty pharmaceutical products through...
Red Orbit (Free subscription) | 11/09/2009
LONDON, November 9 /PRNewswire/ -- Following the provision of clinical and scientific data to the US Food and Drug Administration (FDA), privately owned UK company Daval International Limited (http://www.davalinternational.com) has been informed that its innovative anti-inflammatory agent AIMSPRO(R) has been awarded an Orphan-Drug designation for the treatment of Amyotrophic Lateral Sclerosis (ALS)....
Medical News Today (Free subscription) | 11/08/2009
Medical News Today (Free subscription) | 11/06/2009
Sunesis Pharmaceuticals, Inc. (Nasdaq: SNSS) announced that the U.S. Food and Drug Administration has granted voreloxin orphan drug designation for the treatment of acute myeloid leukemia (AML).
Sacramento Bee (Free subscription) | 11/06/2009
Antelope resident Patrice Broussard has returned to work and motherhood after a liver transplant. Life is back to normal, she says, except for the 20 pills she takes daily. She also now acts as an ambassador for Golden State Donor Services, a nonprofit agency facilitating organ donations. Television may be blamed for a litany of modern plagues but for one local woman it saved her life. Early this...
Living on the frontlines (Free subscription) | 11/05/2009
Below is a press release from Intermune, the company that produces Pirfenidone, the drug the NIH was studying to treat the pulmonary fibrosis of HPS. I thought HPS'ers might like to know that even though our study didn't reach a conclusion, Intermune is going ahead with the results from the IPF trial and seeking FDA approval. That means that if the FDA finds the drug is safe, and if they are convinced...
The 3 latest articles published by users on Rare diseases :
aarkstore | 10/21/2009
In order to raise public awareness, 29 February 2008 was dedicated the first European rare disease day (‘a rare day for very special people’), but European payers need no reminding of the significance of rare disease treatments, generally known as orphan drugs. Eight years earlier, EU Regulation 141/2000 was enacted to encourage R&D in rare diseases and increase orphan drug output. By any standard...
aarkstore | 09/17/2009
In order to raise public awareness, 29 February 2008 was dedicated the first European rare disease day (‘a rare day for very special people’), but European payers need no reminding of the significance of rare disease treatments, generally known as orphan drugs. Eight years earlier, EU Regulation 141/2000 was enacted to encourage R&D in rare diseases and increase orphan drug output. By any standard...
wbishop10 | 09/15/2009
Watch Fringe Season 2 Online Fringe the American science fiction television series is back for its second season on FOX network from September 17,2009 at 9.00 pm, created by J.J.Abrams, Alex Kurtzman and Robert Orci ,fringe follows the exploits of the FBI Fringe Division team based in Boston and headed by special agents Olivia Dunham, mad scientist Walter Bishop and his son “ jack of all trades” Peter...
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